CROMSOURCE’s overall therapeutic expertise includes the management of pharmaceutical trials in a variety of rare disease indications. With proven expertise in finding and recruiting the right patients for these challenging studies, CROMSOURCE supports such projects with our trusted methodology, which involves detailed project planning, protocol assessment, logistical analysis and the execution of all aspects of your clinical trial.
Most often, the major challenges inherent to rare diseases studies is a limited patient population with a wide geographical spread. In order to address these challenges, the first step is to conduct a thorough feasibility analysis. With our Feasibility Plus approach, our deep connections with advocacy groups and our global coverage, CROMSOURCE is able to anticipate and address all of the operational obstacles and provide our clients with innovative and reliable solutions to successfully manage their clinical projects.
CROMSOURCE’s Rare Disease & Orphan Drug experience includes a history of nearly 50 studies in a broad range of indications, including but not limited to:
- Acute Leukemia
- Alpha-1 antitrypsin deficiency
- Amyotrophic Lateral Sclerosis
- Cystic fibrosis
- Duchenne Muscular Dystrophy
- Limbal Stem Cell Deficiency
- Malignant Melanoma
- Multiple Sclerosis
- Multiple System Atrophy
- Myasthenia Gravis
- Neurotrophic Keratitis
- Retinitis pigmentosa
- Rhesus Disease
February 28th is Rare Disease Day Worldwide
On February 28, 2023, Rare Disease Day will be celebrated to spread awareness and advocacy of rare disease and those affected by rare disease every single day.
At CROMSOURCE we are dedicated to supporting those pharma companies in the clinical development of new treatments for rare diseases.
We are aware of how devastating these diseases are for patients and families and for this reason we want to join in this world-wide initiative to spread awareness!
Living with a Rare Disease
Many of these diseases are devastating and severely impact the patient’s life. Knowing of her involvement with the “Fondazione per la Ricerca sulla Fibrosi Cistica – Onlus” (Italian Cystic Fibrosis Research Foundation), our very own Francesca Farma, Business Development Director at CROMSOURCE kindly shared her video as a mother of a son who is living with Cystic Fibrosis, a rare disease.